Neurology ReviewsThe dawning age of therapy for Friedreich ataxiaOctober 13, 2023Neuromuscular DisordersRare Diseases
Neurology ReviewsAdvances in testing and therapeutics are improving the lives of patients with Fabry diseaseOctober 13, 2023Rare Diseases
Neurology ReviewsThe Orphan Drug Act and NORD at their 40th anniversary: Dramatic achievements and ongoing innovationOctober 13, 2023Rare Diseases
Neurology ReviewsEmerging therapies in Duchenne and facioscapulohumeral muscular dystrophyOctober 13, 2023Rare DiseasesNeuromuscular Disorders
Neurology ReviewsHas prompt diagnosis of amyotrophic lateral sclerosis become urgent?October 13, 2023Rare DiseasesNeuromuscular Disorders
Neurology ReviewsGene therapy promising for reversal of hereditary vision lossJuly 14, 2023Rare Diseases
Neurology ReviewsMyasthenia gravis drug gets FDA nodJune 27, 2023Myasthenia GravisRare DiseasesNeuromuscular Disorders
Neurology ReviewsCan a repurposed Parkinson’s drug slow ALS progression?June 22, 2023Movement DisordersRare DiseasesParkinson's Disease
Neurology ReviewsU.S. incidence, prevalence of myasthenia gravis is risingMay 3, 2023Myasthenia GravisRare DiseasesNeuromuscular Disorders
Neurology ReviewsStudy compares noninvasive treatments of cutaneous neurofibromasApril 15, 2023Rare Diseases