The Rare Pediatric Diseases Special Report is a supplement to Pediatric News that discusses advancements in the treatment of rare pediatric neuromuscular disorders like spinal muscular atrophy, Duchenne muscular dystrophy, and X-linked myotubular myopathy, as well as epileptic encephalopathies that occur in infancy and early childhood, such as West syndrome, Lennox-Gastaut syndrome, and Dravet syndrome.
